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pubmed-article:9545360pubmed:abstractTextGloboid-cell leukodystrophy is caused by a deficiency of galactocerebrosidase, which results in progressive central nervous system deterioration. We investigated whether allogeneic hematopoietic stem-cell transplantation can provide a source of leukocyte galactocerebrosidase and thereby prevent the decline of central nervous system function in patients with the disease.lld:pubmed
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pubmed-article:9545360pubmed:articleTitleHematopoietic stem-cell transplantation in globoid-cell leukodystrophy.lld:pubmed
pubmed-article:9545360pubmed:affiliationDepartment of Pediatrics, University of Minnesota School of Medicine, Minneapolis, USA.lld:pubmed
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